MIT Technology Review @techreview A media company making technology a greater force for good. Get our journalism: go.technologyreview.com/newsletters Nov. 19, 2019 1 min read

The era of editing human genes to treat inherited disease has arrived.  http://bit.ly/2XtAs1y 

A pair of biotech companies that say they’ve eliminated painful symptoms from two patients with blood diseases.  http://ir.crisprtx.com/news-releases/news-release-details/crispr-therapeutics-and-vertex-announce-positive-safety-and 

The beta thalassemia patient, for instance, who lives in Europe, used to receive about 16 blood transfusions a year but hasn’t needed one since the treatment.

According to @NPR, the sickle-cell patient no longer suffers from pain attacks.

“This preliminary data shows for the first time that gene editing has actually helped a patient with sickle-cell disease” - Haydar Frangoul of the @SarahCannonDocs  https://www.npr.org/sections/health-shots/2019/11/19/780510277/gene-edited-supercells-make-progress-in-fight-against-sickle-cell-disease 

*Both patients did suffer some serious side effects, because their immune systems needed to be mostly destroyed with chemotherapy before the repaired bone marrow cells were reinfused.  https://www.technologyreview.com/f/614736/companies-declare-signs-of-success-in-crispr-treatment-of-blood-disorders/ 

*For now, the biotechs don’t want to talk about the costs. Samarth Kulkarni, CEO of CRISPR Therapeutics, told @Forbes it is “too early to contemplate any sort of pricing decisions.”  https://www.forbes.com/sites/leahrosenbaum/2019/11/19/human-crispr-trials-promising/#384ac60e2daa 


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